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The collaboration aim to discover and provide experimental antisense oligonucleotide (ASO) medicines to nano-rare disease patients (1 to 30 patients worldwide) for free, for life.
Lead Product(s): Antisense Oligonucleotide
Therapeutic Area: Rare Diseases and Disorders Product Name: Undisclosed
Highest Development Status: Discovery Product Type: Large molecule
Partner/Sponsor/Collaborator: n-Lorem Foundation
Deal Size: Undisclosed Upfront Cash: Undisclosed
Deal Type: Partnership February 08, 2022