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Find Novel Drugs for Genetic Disease under Development
Details :
Fosigotifator is a Other Small Molecule drug candidate, which is currently being evaluated in clinical studies for the treatment of Leukoencephalopathies.
Details :
Eicosapentaenoic Acid|Docosahexaenoic Acid is a Dietary Supplement drug candidate, which is currently being evaluated in Undisclosed clinical studies for the treatment of Frail Elderly Syndrome.
Product Name : Undisclosed
Product Type : Dietary Supplement
Upfront Cash : Inapplicable
September 19, 2025
Lead Product(s) :
Eicosapentaenoic Acid|Docosahexaenoic Acid
Details :
Advanz secures exclusive rights from Alvotech to commercialize three biosimilar candidates, Ilaris (canakinumab), Kesimpta (ofatumumab) and an undiclosed biosimilar in Europe.
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GMP Intervention Product is a Dietary Supplement drug candidate, which is currently being evaluated in clinical studies for the treatment of Phenylketonurias.
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Tyrosol is a Plant Extract/Herbal drug candidate, which is currently being evaluated in clinical studies for the treatment of Creatine Deficiency Syndromes.
Details :
Apitegromab is a Antibody drug candidate, which is currently being evaluated in clinical studies for the treatment of Muscular Atrophy, Spinal.
Details :
Plozasiran is a Oligonucleotide drug candidate, which is currently being evaluated in clinical studies for the treatment of Hyperlipoproteinemia Type I.
Details :
GCB-001 is a drug candidate, which is currently being evaluated in clinical studies for the treatment of Spinal Muscular Atrophies of Childhood.