

Boost your online visibility by uploading your products, APIs, FDFs, intermediates, excipients, and services for free on PharmaCompass.
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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : $345.0 million
Deal Type : Public Offering
uniQure Announces Closing of Upsized Public Offering
Details : uniQure intends to use the net proceeds to fund its commercialization readiness activities, the potential commercial launch of AMT-130, a one-time gene therapy for Huntington's disease.
Product Name : AMT-130
Product Type : Cell & Gene Therapy
Upfront Cash : Undisclosed
September 29, 2025
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : $345.0 million
Deal Type : Public Offering

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Hercules Capital
Deal Size : Undisclosed
Deal Type : Financing
Uniqure Secures $125M Non-Dilutive Funding, Refinances $50M Debt
Details : The financing deal will support the development of AMT-130, a gene therapy for the treatment of Huntington’s disease.
Product Name : AMT-130
Product Type : Cell & Gene Therapy
Upfront Cash : Undisclosed
September 24, 2025
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Hercules Capital
Deal Size : Undisclosed
Deal Type : Financing

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
uniQure gets FDA Breakthrough Therapy Tag for AMT-130 in Huntington’s Disease
Details : AMT-130 lowers both normal and mutant huntingtin protein, currently being investigated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
April 17, 2025
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : $75.0 million
Deal Type : Public Offering
uniQure Announces Pricing of its Public Offering
Details : The net proceeds will support the company to advance its AMT-130, which is being evaluated for the treatment of patients suffering from Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Undisclosed
January 08, 2025
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : $75.0 million
Deal Type : Public Offering

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : Undisclosed
Deal Type : Public Offering
uniQure Announces Proposed Public Offering
Details : The net proceeds will support the company to advance its AMT-130, which is being evaluated for the treatment of patients suffering from Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Undisclosed
January 07, 2025
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Leerink Partners
Deal Size : Undisclosed
Deal Type : Public Offering

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
uniQure Alignment with FDA on Accelerated Approval for AMT-130 in Huntington’s Disease
Details : AMT-130 is an mHTT production inhibitor cell and gene therapy drug candidate, which is currently being evaluated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
December 10, 2024
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
uniQure Announces Positive Data for AMT-130 in Huntington Disease Trials
Details : AMT-130 is an mHTT production inhibitor cell and gene therapy drug candidate, which is currently being evaluated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
July 09, 2024
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
uniQure Reports Positive Interim Data for AMT-130 in Huntington Disease Trials
Details : AMT-130 is an mHTT production inhibitor cell and gene therapy drug candidate, which is currently being evaluated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
July 09, 2024
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
uniQure Receives FDA RMAT Designation for AMT-130 in Huntington’s Disease
Details : AMT-130 is an mHTT production inhibitor cell and gene therapy drug candidate, which is currently being evaluated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
June 03, 2024
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : AMT-130 is an mHTT production inhibitor cell and gene therapy drug candidate, which is currently being evaluated for the treatment of Huntington’s disease.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
December 19, 2023
Lead Product(s) : Antimony pentoxide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
