Company profile for GeneTx Biotherapeutics

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GeneTx Biotherapeutics was setup as a subsidiary of the Foundation for Angelman Syndrome Therapeutics for the development and commercialization of an investigational antisense drug, GTX-102, for the treatment of Angelman syndrome (AS). Angelman syndrome (AS) is a rare genetic disorder that affects approximately one in 15,000 live births. AS is caused by a loss of function of the maternally inherited UBE3A gene. Symptoms of AS ...
GeneTx Biotherapeutics was setup as a subsidiary of the Foundation for Angelman Syndrome Therapeutics for the development and commercialization of an investigational antisense drug, GTX-102, for the treatment of Angelman syndrome (AS). Angelman syndrome (AS) is a rare genetic disorder that affects approximately one in 15,000 live births. AS is caused by a loss of function of the maternally inherited UBE3A gene. Symptoms of AS include developmental delay, impaired motor function, loss of speech, and epilepsy. GeneTx Biotherapeutics’ GTX-102 is designed to compensate for the deficiencies that result from the underlying genetic causes.

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CONTACT DETAILS

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Country
Country
U.S.A
Address
Address
5020 Clark Road, #240 Sarasota, FL 34233
Telephone
Telephone
+1 (630) 639-7271
Linkedin
Linkedin
youtube
YouTube
Twitter
Twitter

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NEWS #PharmaBuzz

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https://www.globenewswire.com/news-release/2022/07/18/2481331/20739/en/Ultragenyx-and-GeneTx-Provide-Program-Update-on-GTX-102-for-Angelman-Syndrome-Including-Promising-Interim-Data-from-Phase-1-2-Study.html

GLOBENEWSWIRE
18 Jul 2022

https://www.streetinsider.com/Corporate+News/Ultragenyx+Pharma+%28RARE%29+and+GeneTx+Issues+Update+on+Phase+12+Clinical+Study+of+GTX-102/19422427.html

STREETINSIDER
06 Jan 2022

https://endpts.com/after-pumping-the-brakes-on-their-angelman-syndrome-study-ultragenyx-and-genetx-are-back-in-the-race/

N. DeFeudis ENDPTS
28 Sep 2021

https://www.clinicaltrialsarena.com/news/genetx-ultragenyx-angelman-syndrome-trial/

CLINICAL TRAILS ARENA
11 Jun 2021

https://www.globenewswire.com/news-release/2021/05/19/2232478/20739/en/GeneTx-and-Ultragenyx-Receive-Clearance-from-Health-Canada-to-Begin-Clinical-Study-of-GTX-102-in-Canada-for-the-Treatment-of-Angelman-Syndrome.html

GLOBENEWSWIRE
18 May 2021
Gene therapy for autism-linked condition weakened legs, robbing two people
Gene therapy for autism-linked condition weakened legs, robbing two people

05 Nov 2020

// Giorgia Guglielmi, Spectrum SCIENCEMAG

https://www.sciencemag.org/news/2020/11/gene-therapy-autism-linked-condition-weakened-legs-robbing-two-people-ability-walk

Giorgia Guglielmi, Spectrum SCIENCEMAG
05 Nov 2020

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