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Details:
Viralgen Vector Core and Elpida Therapeutics partner to manufacture adeno-associated vector serotype 9 (AAV9) based therapies, including MELPIDA, for anticipated Spastic Paraplegia 50 (SPG50) and Charcot-Marie-Tooth disease type 4J (CMT4J) clinical trials.
Lead Product(s): Serotype 9 AAV Therapy
Therapeutic Area: Rare Diseases and Disorders Product Name: MELPIDA
Highest Development Status: Phase I/ Phase II Product Type: Cell and Gene therapy
Partner/Sponsor/Collaborator: Elpida
Deal Size: Undisclosed Upfront Cash: Undisclosed
Deal Type: Partnership September 28, 2023
Details:
Axovant will have access to manufacturing resources for Axovant’s AAV-based gene therapy programs, AXO-AAV-GM1 for GM1 gangliosidosis and AXO-AAV-GM2 for GM2 gangliosidosis with sufficient capacity to support ongoing development and eventual commercialization.
Lead Product(s): AXO-AAV-GM1
Therapeutic Area: Genetic Disease Product Name: AXO-AAV-GM1
Highest Development Status: Phase I/ Phase II Product Type: Cell and Gene therapy
Partner/Sponsor/Collaborator: Sio Gene Therapies
Deal Size: Undisclosed Upfront Cash: Undisclosed
Deal Type: Partnership September 15, 2020