Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : Copper Histidine
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase III
Sponsor : Fortress Biotech
Deal Size : Inapplicable
Deal Type : Inapplicable
Sentynl Therapeutics Announces FDA Acceptance of CUTX-101 for Menkes Disease
Details : CUTX-101 is a subcutaneous injectable formulation of copper histidinate, which is being evaluated for the treatment of menkes disease.
Product Name : CUTX-101
Product Type : Vitamins/Minerals/Inorganic Salts
Upfront Cash : Inapplicable
January 06, 2025
Lead Product(s) : Copper Histidine
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase III
Sponsor : Fortress Biotech
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : Fosdenopterin
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Approved FDF
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Sentynl Receives MHRA Authorization for NULIBRY® in MoCD Type A
Details : Nulibry (fosdenopterin) is the first therapy for patients in Great Britain with molybdenum cofactor deficiency Type A, an ultra-rare genetic disorder that often progresses rapidly in infants.
Product Name : Nulibry
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
April 16, 2024
Lead Product(s) : Fosdenopterin
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Approved FDF
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable