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Disease","country":"U.S.A","productType":"Cell and Gene therapy","year":"2023","type":"Inapplicable","leadProduct":"Delandistrogene Moxeparvovec","moa":"Micro-dystrophin gene","graph1":"Genetic Disease","graph2":"Phase III","graph3":"Sarepta Therapeutics","amount2":0,"highestDevelopmentShortName":"Ph III","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Infusion","sponsorNew":"Sarepta Therapeutics \/ Inapplicable","highestDevelopmentStatusID":"10","companyTruncated":"Sarepta Therapeutics \/ Inapplicable"}]

Find Clinical Drug Pipeline Developments & Deals by Sarepta Therapeutics

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                          Therapeutic Area by Lead Product

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                          Top Deals by Deal Size (USD bn)

                          01

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec) is a single-dose gene transfer therapy, designed to to treat Duchenne muscular dystrophy by producing micro-dystrophin in skeletal muscle.

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          January 27, 2025

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Approved FDF

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          02

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : SRP-9003 (bidridistrogene xeboparvovec) is an investigational gene therapy that uses the AAVrh74 vector. It is being evaluated for the treatment of limb-girdle muscular dystrophy type 2E/R4.

                          Product Name : SRP-9003

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          December 18, 2024

                          Lead Product(s) : Bidridistrogene Xeboparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase III

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          03

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec) is a single-dose gene transfer therapy designed to address the underlying cause of DMD through the targeted production of micro-dystrophin in skeletal muscle.

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          June 20, 2024

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Approved FDF

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          04

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec) is a single-dose, AAV based gene transfer therapy for intravenous infusion designed to address the underlying genetic cause of Duchenne muscular dystrophy.

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          June 20, 2024

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Approved FDF

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          05

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec) is a single-dose, adeno-associated virus-based gene transfer therapy being evaluated for Duchenne muscular dystrophy with DMD gene mutation.

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          February 16, 2024

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Approved FDF

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          06

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : SRP-5051 (vesleteplirsen) is a next-gen exon-skipping therapy in Phase 2 for Duchenne muscular dystrophy patients amenable to exon 51 skipping.

                          Product Name : SRP-5051

                          Product Type : Peptide

                          Upfront Cash : Inapplicable

                          January 29, 2024

                          Lead Product(s) : Vesleteplirsen

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase II

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          07

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : SRP-9003 (bidridistrogene xeboparvovec) is an investigational gene therapy that uses the AAVrh74 vector. Being evaluated in phase 3 clinical studies for limb-girdle muscular dystrophy type 2E/R4.

                          Product Name : SRP-9003

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          January 16, 2024

                          Lead Product(s) : Bidridistrogene Xeboparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase III

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          08

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec-rokl) is a single-dose, adeno-associated virus (AAV) based gene transfer therapy for intravenous infusion designed to address the underlying genetic cause of Duchenne muscular dystrophy

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          December 22, 2023

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase III

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          09

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : SRP-9001 (delandistrogene moxeparvovec) is an investigational gene transfer therapy intended to deliver SRP-9001 to muscle tissue for the targeted production of essential components of dystrophin.

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          December 05, 2023

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase III

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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                          10

                          Iran Expo
                          Not Confirmed
                          Iran Expo
                          Not Confirmed

                          Details : Elevidys (delandistrogene moxeparvovec) is a single-dose gene transfer therapy for intravenous infusion designed to address the underlying cause of Duchenne muscular dystrophy through the targeted production of ELEVIDYS micro-dystrophin in skeletal muscl...

                          Product Name : Elevidys

                          Product Type : Cell and Gene therapy

                          Upfront Cash : Inapplicable

                          October 30, 2023

                          Lead Product(s) : Delandistrogene Moxeparvovec

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase III

                          Sponsor : Inapplicable

                          Deal Size : Inapplicable

                          Deal Type : Inapplicable

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