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Find Clinical Drug Pipeline Developments & Deals for Migalastat
The proceeds will be used to fund the ongoing operations of the company, including Galafold (migalastat), a small molecule and the first and only oral therapy for adults with Fabry disease and an amenable GLA variant.
New U.S. patent titled “Methods of Treating Fabry Patients Having Renal Impairments” is directed to a molecule comprising Galafold (migalastat) bound to an alpha-galactosidase A protein, it now includes 35 issued patents, 18 of which expire in 2038.
Amicus expects to use the net proceeds in the global commercialization of Galafold for Fabry disease through geographic and label expansion, as well as support for diagnostic initiatives and the anticipated global launch of AT-GAA.