Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : MVX-220
Therapeutic Area : Rare Diseases and Disorders
Study Phase : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
MavriX Wins IND Clearance for Gene Therapy in Angelman Syndrome Trial
Details : MVX-220 is an investigational hu68AAV gene therapy designed to deliver the human UBE3A gene to neurons of the brain with a single intra-cisterna magna (ICM) injection.
Product Name : MVX-220
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
May 12, 2025
Lead Product(s) : MVX-220
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable