Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : GIVI-MPC
Therapeutic Area : Genetic Disease
Study Phase : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
IPS HEART Granted Orphan Drug Designation in the EU for Becker Muscular Dystrophy
Details : GIVI-MPCs derived from pluripotent stem cells form new skeletal muscle with 100% full-length human dystrophin for DMD and BMD.
Product Name : GIVI-MPC
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
May 14, 2025
Lead Product(s) : GIVI-MPC
Therapeutic Area : Genetic Disease
Highest Development Status : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : ISX9-CPC
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : ISX9-CPC Stem Cell Therapy creates new cardiac muscle and replaces dead scar tissue and restore cardiac function, which is investigated for the treatment of Cardiomyopathy Associated with Danon disease.
Product Name : ISX9-CPC
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
June 07, 2023
Lead Product(s) : ISX9-CPC
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : GIVI-MPC
Therapeutic Area : Genetic Disease
Study Phase : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : GIVI-MPC, a stem cell therapy to create new muscle with full-length dystrophin in Duchenne muscular dystrophy (DMD). It uses givinostat to reprogram human iPSCs into new muscle tissue.
Product Name : GIVI-MPC
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
February 22, 2023
Lead Product(s) : GIVI-MPC
Therapeutic Area : Genetic Disease
Highest Development Status : Preclinical
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable