Drugs in Dev.
Genetic Disease
Phase II/ Phase III
Denmark 
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Lead Product(s) : Etavopivat
Therapeutic Area : Genetic Disease
Study Phase : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
HIBISCUS Study Data Shows Etavopivat Reduces Sickle Cell Disease Crises
Details : FT-4202 (etavopivat) is a Pyruvate kinase isozymes R/L activator, which is being evaluated in adults and adolescents With sickle cell disease.
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : Inapplicable
December 07, 2024
Lead Product(s) : Etavopivat
Therapeutic Area : Genetic Disease
Highest Development Status : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Navepegritide
Therapeutic Area : Genetic Disease
Study Phase : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : TransCon CNP (Navepegritide) is a Peptide drug candidate, which is currently being evaluated in phase II/ phase III clinical studies for the treatment of Achondroplasia.
Product Name : TransCon CNP
Product Type : Peptide, Unconjugated
Upfront Cash : Inapplicable
July 03, 2023
Lead Product(s) : Navepegritide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Dasiglucagon
Therapeutic Area : Genetic Disease
Study Phase : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Zealand Pharma Submits New Drug Application to US FDA for Dasiglucagon in Congenital Hyperinsulinism
Details : ZP4207 (dasiglucagon) subcutaneous injection is a glucagon receptor agonist and indicated for the treatment of severe hypoglycemia in pediatric and adult patients with diabetes aged 6 years and above.
Product Name : Zegalogue
Product Type : Hormone
Upfront Cash : Inapplicable
June 30, 2023
Lead Product(s) : Dasiglucagon
Therapeutic Area : Genetic Disease
Highest Development Status : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Navepegritide
Therapeutic Area : Genetic Disease
Study Phase : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : TransCon CNP (Navepegritide) is a Peptide drug candidate, which is currently being evaluated in phase II/ phase III clinical studies for the treatment of Achondroplasia.
Product Name : TransCon CNP
Product Type : Peptide, Unconjugated
Upfront Cash : Inapplicable
October 28, 2022
Lead Product(s) : Navepegritide
Therapeutic Area : Genetic Disease
Highest Development Status : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Dasiglucagon
Therapeutic Area : Genetic Disease
Study Phase : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Trial Evaluating Efficacy and Safety of Dasiglucagon in Children With Congenital Hyperinsulinism
Details : Dasiglucagon is a Hormone drug candidate, which is currently being evaluated in phase II/ phase III clinical studies for the treatment of Congenital Hyperinsulinism.
Product Name : Undisclosed
Product Type : Hormone
Upfront Cash : Inapplicable
November 21, 2019
Lead Product(s) : Dasiglucagon
Therapeutic Area : Genetic Disease
Highest Development Status : Phase II/ Phase III
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
