Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : Allogeneic Processed Thymus Tissue
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Approved FDF
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : RETHYMIC® (allogeneic processed thymus tissue-agdc), one-time regenerative tissue-based therapy for immune reconstitution in pediatric with congenital athymia. RETHYMIC is engineered human thymus tissue designed to regenerate thymic function children wi...
Product Name : Rethymic
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
August 10, 2021
Lead Product(s) : Allogeneic Processed Thymus Tissue
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Approved FDF
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : Recombinant Human Acid Ceramidase
Therapeutic Area : Genetic Disease
Study Phase : IND Enabling
Sponsor : Aceragen
Deal Size : $226.0 million
Deal Type : Acquisition
Aceragen Launches with Acquisition of Enzyvant‘s Investigational Therapy for Farber Disease
Details : ACG-801 is an investigational form of recombinant human acid ceramidase (rhAC) designed to address the genetic deficiency of the naturally occurring enzyme which is the cause of Farber disease and Spinal Muscular Atrophy with Progressive Myoclonic Epilep...
Product Name : ACG-801
Product Type : Enzyme
Upfront Cash : Undisclosed
March 05, 2021
Lead Product(s) : Recombinant Human Acid Ceramidase
Therapeutic Area : Genetic Disease
Highest Development Status : IND Enabling
Sponsor : Aceragen
Deal Size : $226.0 million
Deal Type : Acquisition