Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : BFB-101
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
FDA approves trial to advance treatment for Hereditary Spastic Paraplegia (HSP)
Details : BFB-101 is an AP4B1 gene therapy candidate, which is currently being evaluated for the treatment of Hereditary Spastic Paraplegia.
Product Name : BFB-101
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
May 07, 2025
Lead Product(s) : BFB-101
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : BFB-101
Therapeutic Area : Genetic Disease
Study Phase : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
BlackfinBio gets FDA IND for SPG47 Gene Therapy BFB-101 Phase 1/2 Trial
Details : BFB-101 aims to address the underlying genetic cause of hereditary spastic paraplegia, Type 47 (SPG47) by delivering a functional copy of the AP4B1 gene.
Product Name : BFB-101
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
April 28, 2025
Lead Product(s) : BFB-101
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable