All News #Library
Rare Diseases
Vertex Gets FDA Label Expansion For Alyftrek And Trikafta
01 Apr 2026 //
PHARMIWEB
Vertex Win 2025 Lasker DeBakey Award for Cystic Fibrosis Research
11 Sep 2025 //
PHARMAWEB
CHMP Backs KAFTRIO Label Expansion For Cystic Fibrosis Rare Mutations
28 Feb 2025 //
BUSINESSWIRE
FDA approves Vertex Pharma`s triple combo cystic fibrosis treatment
21 Dec 2024 //
REUTERS
Vertex, beaten by rare disease again, drops 2 assets on growing discard pile
01 Aug 2024 //
FIERCE BIOTECH
As pharma eyes shiny obesity drugs, Vertex tops orphan drug list
24 Apr 2024 //
FIERCE BIOTECH
Ex-Retrophin BD chief flips his rare disease startup onto Nasdaq
24 Sep 2019 //
ENDPTS
FDA fires off a warning on rare cases involving death, adverse liver events
29 Aug 2019 //
ENDPTS
For head of Massachusetts biotech trade group, drug progress is personal
04 Jan 2019 //
STAT NEWS
Vertex to submit Orkambi, Symkevi to SMC
20 Dec 2018 //
PHARMA TIMES
Catalyst will charge $375,000 for rare disease drug
13 Dec 2018 //
STAT NEWS
MPs order release of documents on negotiations for Vertex’ CF drugs
12 Nov 2018 //
PHARMA TIMES
Sanofi, Vertex and more back first rare disease film festival
30 Aug 2017 //
FIERCE PHARMA

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