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Rare Diseases
Neurogene Reveals FDA Breakthrough For NGN-401 In Rett Syndrome
26 Feb 2026 //
BUSINESSWIRE
Neurogene Sets 2026 Milestones for NGN-401 in Rett Syndrome
12 Jan 2026 //
BUSINESSWIRE
Neurogene Reports Positive Data from NGN-401 Gene Therapy Trial
12 Nov 2025 //
BUSINESSWIRE
Neurogene Initiates NGN-401 Gene Therapy Trial For Rett Syndrome
06 Nov 2025 //
BUSINESSWIRE
Neurogene To Start NGN-401 Gene Therapy Trial For Rett Syndrome
09 Oct 2025 //
BUSINESSWIRE
Neurogene Details Death in Rett Syndrome Gene Therapy Trial
17 May 2025 //
FIERCE BIOTECH
Neurogene Introduces Treatment for Rare Hyperinflammatory Syndrome
16 May 2025 //
BUSINESSWIRE
FDA picks Denali, Neurogene and more for rare disease program
04 Jun 2024 //
FIERCE BIOTECH

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