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Rare Diseases
Kyowa Kirin Poised For Windfall With Newborn Screening Update
19 Dec 2025 //
BIOSPACE
Orchard Celebrates Addition of Metachromatic Leukodystrophy
16 Dec 2025 //
GLOBENEWSWIRE
Ultragenyx Sells Future Crysvita Royalties For $400 Million
04 Nov 2025 //
GLOBENEWSWIRE
Kyowa Kirin, Orchard OTL-200 Gets Orphan Designation in Japan
28 Oct 2025 //
GLOBENEWSWIRE
Poteligeo Registry Shows OS Gain in Advanced CTCL Patients
22 Oct 2025 //
PHARMIWEB
Kyowa Kirin, NewBridge To Improve Rare Disease Medicine Access In MENA
08 Aug 2024 //
BIOSPECTRUM ASIA
NICE Enables Access to First Treatment for XLH in Adults
21 Jun 2024 //
BUSINESSWIRE
Kyowa Kirin Responds to NICE’s Publication of Appraisal Document for CRYSVITA
29 Nov 2023 //
BUSINESSWIRE
Kyowa Kirin brings rare disease drug`s marketing back in house, future US growth
03 May 2023 //
ENDPTS
Teva successfully used a rare pediatric PRV to speed the approval for Ajovy
21 Nov 2018 //
RAPS
XLH patients to get routine access to first new therapy in 30 years
10 Oct 2018 //
PHARMA TIMES
NICE u-turn approves funding for rare disease therapy Crysvita
05 Sep 2018 //
PHARMA TIMES
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