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Rare Diseases
FDA Approves WAKIX for Pediatric Cataplexy
17 Feb 2026 //
BUSINESSWIRE
Harmony Biosciences Reveals EPX-100 Efficacy in Dravet Syndrome
08 Dec 2025 //
PHARMIWEB
Harmony Bio Report Ph 3 Zyn002 Study Update in Fragile X Syndrome
24 Sep 2025 //
FIERCE BIOTECH
Harmony Bio to Unveil Rare Epilepsy Data at Epilepsy Congress
26 Aug 2025 //
BUSINESSWIRE
Harmony Biosciences Presents ZYN002 Data in Fragile X Syndrome
08 Apr 2025 //
BUSINESSWIRE
Harmony Biosciences Highlights Late-Stage Pipeline at Investor Day
01 Oct 2024 //
PR NEWSWIRE
Harmony Biosciences Receives FDA Orphan Drug Designation For Pitolisant
20 Feb 2024 //
PR NEWSWIRE
Harmony Biosciences Announces FDA Orphan Drug Designation For Pitolisant
07 Sep 2023 //
PR NEWSWIRE

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