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Rare Diseases
Genethon Advances Gene Therapies For Rare Genetic Diseases
26 Jan 2026 //
BUSINESSWIRE
Genethon Licenses Askbio For Pompe Disease Gene Therapy
14 Jan 2026 //
BUSINESSWIRE
Genethon Shows 2-Year Efficacy In Duchenne Muscular Dystrophy
09 Oct 2025 //
BUSINESSWIRE
Genethon Marks Rare Disease Day With Advances In Gene Therapies
27 Feb 2025 //
BUSINESSWIRE
Genethon, Hansa Begin Phase 2 for Imlifidase in Crigler-Najjar
03 Dec 2024 //
PR NEWSWIRE
Genethon Pursues Strategies for Ensuring Patient Access to Gene Therapies
29 Feb 2024 //
BUSINESSWIRE
Phase 1/2 Trial Results of Genethon’s Gene Therapy for Crigler-Najjar Syndrome
22 Aug 2023 //
BUSINESSWIRE
Genethon Given PRIME Status by EMA for Gene Therapy
07 Mar 2023 //
BUSINESSWIRE

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