All News #Library
Rare Diseases
Roche’s Enspryng cuts relapse risk by 68% in Neuroinflammatory
22 Apr 2026 //
PRESS RELEASE
Genentech Drug Fails Rare Disease Trial, Raises Obesity Risk
20 Mar 2026 //
FIERCE BIOTECH
Another Setback For Enspryng As Roche Halts Duchenne Development
23 Feb 2026 //
FIERCE PHARMA
Biogen Bets HD Spinraza Can Outmuscle Roche`s Oral Rival
06 Feb 2026 //
FIERCE PHARMA
Sobi Tops Roche in Rare Disease Patients` Reputation Rankings
23 Sep 2025 //
FIERCE PHARMA
Roche Halts Elevidys Shipments in Select Non-US Countries
23 Jul 2025 //
BIOSPACE
Roche discontinues low dose in Huntington’s trial
19 Apr 2025 //
ENDPTS
Oak Hill Bio Licenses Angelman Syndrome Treatment to Roche
15 Apr 2025 //
BUSINESSWIRE
FDA approves Roche’s Evrysdi tablet as first & only tablet for SMA
12 Feb 2025 //
GLOBENEWSWIRE
Roche Regains Reputation Crown Among Rare Disease Patient Groups
20 Aug 2024 //
FIERCE PHARMA
CHMP Recommends EU Approval Of Roche’s PiaSky For PNH Blood Condition
28 Jun 2024 //
GLOBENEWSWIRE
Horizon, Roche top list for pharma reputation among rare disease patient groups
22 Aug 2023 //
ENDPTS
Roche May Have A Competing Drug For A Rare Disease
27 Dec 2018 //
SEEKING ALPHA
Emmetuxumab injection for rare disease treatment was approved for marketing
11 Dec 2018 //
CHINA NMPA
Novartis says its top drug prospect is worth $4M-$5M for a once-and-done use
05 Nov 2018 //
ENDPTS
Roche puts down $75M to sign on AMD drug, following Huntington’s deal
11 Oct 2018 //
ENDPTS
FDA Approves Actemra for SJIA - Rare Form of Juvenile Arthritis
14 Sep 2018 //
BUSINESSWIRE
Bayer`s hemophilia A treatment gets U.S. FDA approval
31 Aug 2018 //
REUTERS
AbbVie, J&J score early nod for Imbruvica in rare cancer
27 Aug 2018 //
FIERCE PHARMA
In 3 firsts, Dompe`s eye drop Oxervate wins FDA nod for rare disease
23 Aug 2018 //
PMLIVE
IONIS-HTT Rx (RG6042) Granted PRIME Designation by the EMA
02 Aug 2018 //
PR NEWSWIRE
Azafaros to develop new treatments for rare metabolic disorders
23 Jul 2018 //
BIOSPECTRUM
Abeona taps ex-Alexion CCO as new chief, eyeing commercial ops
03 Apr 2018 //
FIERCE BIOTECH
Rare-Disease Drugmakers Join in Worries Over GOP Health Overhaul
06 Jul 2017 //
BLOOMBERG
Biogen, Roche ink deals with Bristol for rare disease drugs
14 Apr 2017 //
BIOPHARMADIVE

Market Place
Sourcing Support