All News #Library
Rare Diseases
Bayer To Lower Cost Of Eylea 2mg In India For Retinal Disease
02 Apr 2026 //
INDPHARMAPOST
Bayer Ditches 1 AAV Gene Therapy From Pompe Disease Pair
04 Mar 2026 //
FIERCE BIOTECH
Essential Pharma Acquires Ventavis to Bolster Pulmonary Portfolio
17 Feb 2026 //
GLOBENEWSWIRE
Genethon Licenses Askbio For Pompe Disease Gene Therapy
14 Jan 2026 //
BUSINESSWIRE
FDA Accepts AskBio IND for AB-1009 in Pompe Disease LOPD
08 Jan 2026 //
GLOBENEWSWIRE
Bayer Initiates Phase 2 Trial For Alport Syndrome Treatment
04 Dec 2025 //
PHARMIWEB
Bayer cuts PhII orphan drug as it ups R&D spending
08 Aug 2023 //
ENDPTS
TG Therapeutics’ shares jump as umbralisib wins FDA’s breakthrough status
22 Jan 2019 //
ENDPTS
Bayer`s hemophilia A treatment gets U.S. FDA approval
31 Aug 2018 //
REUTERS
Novartis farms out rare disease drug to LifeMax Labs
28 Aug 2018 //
FIERCE BIOTECH

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