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Rare Diseases
Sarepta Challenges Prompt Search For Advancements In DMD Therapy
09 Feb 2026 //
BIOSPACE
Avidity Biosciences Plans Del-Zota Bla Submission For DMD44
13 Oct 2025 //
PR NEWSWIRE
Avidity Bioscience To Present Del-Zota Data In DMD At WMS Society
06 Oct 2025 //
PR NEWSWIRE
Avidity` Del-zota Reverses DMD44 Progression in Phase 1/2 Trial
10 Sep 2025 //
PR NEWSWIRE
Avidity Biosciences to Present Phase 1/2 Fortitude Trial Data
11 Jun 2025 //
PR NEWSWIRE
Avidity gets Orphan Designation in Japan for Myotonic Dystrophy
08 Apr 2025 //
PR NEWSWIRE
Avidity Plans BLA Submission for Rare Muscle Diseases by 2025
08 Jan 2025 //
PR NEWSWIRE
Avidity Announces New Precision Cardiology Development Candidates
12 Nov 2024 //
PR NEWSWIRE
Avidity therapy shows possible benefit in muscular dystrophy
12 Jun 2024 //
FIERCE BIOTECH
Avidity Biosciences Honors Rare Disease Day®
29 Feb 2024 //
PR NEWSWIRE
Avidity Biosciences Honors Rare Disease Day®
28 Feb 2023 //
PR NEWSWIRE
Avidity Receives FDA Orphan Drug Designation for AOC 1020 to treat FSHD
15 Feb 2023 //
PR NEWSWIRE
Avidity Biosciences Receives FDA Orphan Drug Designation for AOC 1020
14 Feb 2023 //
PR NEWSWIRE

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