FDA Proposes to withdraw Amgen`s drug for Rare Autoimmune Disease
27 Apr 2026 //
REUTERS
FDA warns of liver injury cases tied to Amgen`s Rare Disease Drug
31 Mar 2026 //
FDA
EMA Seeks Input On Drafting Myasthenia Gravis Trial Guide
19 Feb 2026 //
RAPS
EU Approves Amgen`s Uplizna for Generalized Myasthenia Gravis
13 Feb 2026 //
PR NEWSWIRE
Amgen Thumbs-Down on FDA’s ask, Tavneos Sales Continue
05 Feb 2026 //
FIERCE PHARMA
FDA Approves Uplizna for Generalized Myasthenia Gravis in Adults
11 Dec 2025 //
PR NEWSWIRE
Rare Disease Clinical Progress Boosts Long-Term Revenue Potential
07 Aug 2025 //
PR NEWSWIRE
Kyowa, Amgen, Sanofi Support Women`s Health Info Update
23 Jul 2025 //
FIERCE PHARMA
FDA approves Amgen`s Uplizna in IgG4-related disease
04 Apr 2025 //
ENDPOINTS
Amgen Presents New Data on Rare Inflammatory Diseases at ACR 2024
14 Nov 2024 //
PR NEWSWIRE
Roche Regains Reputation Crown Among Rare Disease Patient Groups
20 Aug 2024 //
FIERCE PHARMA
Amgen`s drug meets main goal in late-stage study for rare disease
06 Jun 2024 //
REUTERS
US FDA approves Amgen`s biosimilar to AZ`s rare blood disorder treatment
29 May 2024 //
REUTERS
Amgen wants in on obesity. But it`s still working on rare disease, too
23 Feb 2024 //
ENDPTS
Amgen To Host Conference Call On Rare Disease
19 Feb 2024 //
PRESS RELEASE
Horizon Ranks First in Overall Reputation by Rare Disease Patient Groups
23 Aug 2023 //
BUSINESSWIRE
Horizon, Roche top list for pharma reputation among rare disease patient groups
22 Aug 2023 //
ENDPTS
Amgen`s denosumab shows promise in small, NIH-funded rare bone disease study
06 Apr 2023 //
ENDPTS
Amgen dives deeper into rare disease drugs with $27.8 bln Horizon deal
13 Dec 2022 //
REUTERS
Horizon, Jazz, Zogenix are buys at BofA despite threat of copycats
19 Sep 2021 //
SEEKINGALPHA
Horizon partners with MIT for crowdsourced rare disease ideas
18 Sep 2021 //
FIERCEPHARMA
Horizon Reports Record Quarterly Net Sales for Orphan and Rheumatology Segment
08 Aug 2018 //
PRESS RELEASE
Abeona taps ex-Alexion CCO as new chief, eyeing commercial ops
03 Apr 2018 //
FIERCE BIOTECH
Canada probes Horizon Pharma over efforts to boost sales of a rare disease drug
26 Mar 2018 //
STAT NEWS
Horizon Gift Establishes First Clinical Team Endowment Rare Disease Institute
26 Feb 2018 //
GLOBENEWSWIRE
Horizon Pharma plc Partners with Global Genes to Unite the Rare Disease
21 Jun 2017 //
NASDAQ
Horizon Partners with Global Genes® to Unite the Rare Disease Community
20 Jun 2017 //
PRESS RELEASE
Horizon Pharma plc Announces Agreement to Sell European Marketing Rights to PROCYSBI
23 May 2017 //
NASDAQ
Building an orphan pipeline, Horizon Pharma bags Ph3-ready RD drug in $145M
08 May 2017 //
ENDPTS
Tapping into the rare disease market
11 Mar 2017 //
BIO PHARMA DIVE
More Rare Disease Deal making to Follow Horizon`s Raptor Deal
13 Sep 2016 //
THE STREET
Horizon Receives Health Canada Approval for Ravicti
21 Mar 2016 //
MARKET WIRED

Market Place
Sourcing Support