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Rare Diseases
NICE relents and okays Akcea’s rare disease drug Waylivra for NHS use
21 Sep 2020 //
PHARMA PHORUM
Akcea taps first commercial chief as Waylivra debuts and pipeline advances
05 Nov 2019 //
FIERCEP PHARMA
FDA rejects rare disease drug developed by Cambridge`s Akcea
28 Aug 2018 //
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