All News #Library
Rare Diseases
Agios Advances Mitapivat Toward SCD Accelerated Approval
31 Mar 2026 //
GLOBENEWSWIRE
Agios Details 2026 Strategy To Boost Rare Disease Portfolio
12 Jan 2026 //
GLOBENEWSWIRE
FDA Approves Agios` AQVESME For Anemia In Adult Thalassemia
23 Dec 2025 //
GLOBENEWSWIRE
Agios Provides Update on U.S. sNDA for Mitapivat in Thalassemia
08 Dec 2025 //
GLOBENEWSWIRE
Agios’ Pyrukynd turns in mixed results in sickle cell ph. 3
20 Nov 2025 //
GLOBENEWSWIRE
Agios’ Pyrukynd turns in mixed results in sickle cell ph. 3
19 Nov 2025 //
GLOBENEWSWIRE
Agios To Unveil Mitapivat Data In Rare Blood Disorders
03 Nov 2025 //
GLOBENEWSWIRE
Agios` Mitapivat Gets CHMP Nod For Adult with Thalassemia
17 Oct 2025 //
GLOBENEWSWIRE
Avanzanite Partner Agio Receives Positive Opinion for Pyrukynd
17 Oct 2025 //
PHARMIWEB
Agios Updates U.S. PDUFA for Pyruknd in Thalassemia
04 Sep 2025 //
GLOBENEWSWIRE
Agios Wins Saudi Approval for Pyrukynd in Adult Thalassemia
04 Aug 2025 //
GLOBENEWSWIRE
Avanzanite partners Agios to launch Pyrukynd in Europe
09 Jun 2025 //
BUSINESSWIRE
Agios’ Ph 3 Activate-Kids Hits Primary Endpoint In PK Deficiency
13 Feb 2025 //
GLOBENEWSWIRE
Agios Announces 2025 Milestones For Rare Disease Portfolio
13 Jan 2025 //
GLOBENEWSWIRE
FDA Accepts Agios PYRUKYND NDA For Alpha, Beta-Thalassemia Patients
08 Jan 2025 //
GLOBENEWSWIRE
Europe Grants Orphan Status for Mitapivat in Sickle Cell
18 Dec 2024 //
GLOBENEWSWIRE
Agios Presents New Data on Mitapivat & Tebapivat at ASH 2024
05 Nov 2024 //
GLOBENEWSWIRE
Agios Reports Business Highlights and Q3 2024 Financial Results
31 Oct 2024 //
GLOBENEWSWIRE
Agios To Present At Cantor Global Healthcare Conference
05 Sep 2024 //
GLOBENEWSWIRE
Agios Reports Business Highlights and Second Quarter 2024 Financial Results
01 Aug 2024 //
GLOBENEWSWIRE
Agios Announces Phase 3 ACTIVATE-KidsT Study Results
01 Aug 2024 //
GLOBENEWSWIRE
Agios Announces Key Anticipated 2024 Milestones Across Rare Disease Portfolio
08 Jan 2024 //
GLOBENEWSWIRE
Agios to Present Broad Set of Translational Data in Rare Blood Disorders
02 Nov 2023 //
GLOBENEWSWIRE
Agios Launches “Red Cell Revolution†in Recognition of Rare Disease Day
28 Feb 2023 //
GLOBENEWSWIRE

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