First Clinical Trial Results of Gene Therapy (GNT0004) for Duchenne Muscular Dystrophy Presented at International Myology 2024 Congress
Genethon Pursues Strategies for Ensuring Patient Access to Gene Therapies
Genethon Announces Publication of Clinical Trial Results of a Gene Therapy
Positive Phase 1/2 Clinical Trial Results of Genethon’s Gene Therapy for Crigler-Najjar Syndrome, a Rare Liver Disease, Published in The New England Journal of Medicine
PARIS--(BUSINESS WIRE)--Genethon, a pioneer in gene therapy, said today the French government’s support of the GenoTher Biocluster validates the efforts of its founding organizations in creating a global center of excellence in gene therapy and establishes their work and dedication as a national priority for advancing gene therapies to treat both rare and common diseases.
Genethon Given PRIME Status by EMA for Gene Therapy To Treat Crigler-Najjar Syndrome, a Rare Liver Disease
Genethon Launches Pivotal Clinical Trial of Gene Therapy for Crigler-Najjar Syndrome, a Rare Liver Disease
Rather than continue to plug away at individual studies and try to figure out why these side effects were happening in certain patients, Pfizer, Sarepta, Genethon and Solid Biosciences teamed up for a pooled safety analysis (PDF) that was presented this week at the American Society of Gene and Cell Therapy meeting. The companies shared clinical and laboratory data and put together a panel of experts to take a look with the goal of minimizing further medical complications.