The National Institute for Health and Care Excellence (NICE) has published draft guidance for public consultation which does not recommend Vimizin (elosulfase alfa) for the treatment of mucopolysaccharidosis type 4A, also known as MPS 4A and Morquio A syndrome.
BioMarin's Vimizim (elosulfase alfa) Receives Supplemental Approval in US
BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) announced today that Vimizim® (elosulfase alfa) has been approved by the National Medical Products Administration (NMPA) for the treatment of patients with mucopolysaccharidosis type IVA (MPS IVA), also known as Morquio A syndrome. Vimizim is the first treatment in China approved for this condition.
BioMarin had its first manufacturing site outside of the U.S. approved just last year. But the genetic disease specialist is already expanding the site in Ireland and adding dozens of new jobs.