CAMBRIDGE, Mass., May 2, 2024 /PRNewswire/ -- Blueprint Medicines Corporation (Nasdaq: BPMC) today reported financial results, provided a business update for the first quarter ended March 31, 2024, and provided updated financial guidance.
Blueprint Medicines Highlights AYVAKIT® (avapritinib) Long-Term Efficacy and Safety Data and Advances in Mast Cell Disease Research at 2024 AAAAI Annual Meeting
With another quarter exceeding analysts’ expectations, Blueprint Medicines has raised its peak sales estimate for rare disease drug Ayvakit to $2 billion.
EC approves treatment for rare haematological disorder
Blueprint Medicines' AYVAKYT® (avapritinib) Receives Positive CHMP Opinion
Venlo, the Netherlands, and Germantown, Maryland, Aug. 07, 2023 (GLOBE NEWSWIRE) -- QIAGEN (NYSE: QGEN; Frankfurt Prime Standard: QIA) today announced the U.S. Food and Drug Administration (FDA)...
CAMBRIDGE, Mass., May 22, 2023 /PRNewswire/ -- Blueprint Medicines Corporation (Nasdaq: BPMC) today announced that the U.S. Food and Drug Administration (FDA) has approved AYVAKIT® (avapritinib) for the treatment of adults with indolent systemic mastocytosis (ISM). All U.S. patients with ISM now have access to the first and only approved medicine designed to treat their disease.
Blueprint Medicines presented the full dataset for its drug Ayvakit at a medical conference over the weekend as it heads towards an FDA decision in May. Blueprint is hoping to expand Ayvakit’s label into a less advanced form of systemic mastocytosis, a rare disease in which too many mast cells, a type of white blood cell, build up in the body.
Stomach cancer may be a bust for Blueprint Medicines’ Ayvakit, but now the kinase inhibitor is nearing a potential FDA label expansion in a rare blood disorder. The company hopes this use can catapult the drug into blockbusterland.
Blueprint Medicines to Present Positive Data from PIONEER Trial of AYVAKIT® (avapritinib) in Indolent Systemic Mastocytosis at 2023 AAAAI Annual Meeting