Drugs in Dev.
Genetic Disease
Phase I
Spain 
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Lead Product(s) : CTH120
Therapeutic Area : Genetic Disease
Study Phase : Phase I
Sponsor : Hospital del Mar Research Institute (IMIM) | Adknoma | Ministry of Science and Innovation, Spain
Deal Size : Inapplicable
Deal Type : Inapplicable
CTH120 First-in-Human Study: Single and Multiple Ascending Doses and Potential Food Interaction
Details : CTH120 is a drug candidate, which is currently being evaluated in phase I clinical studies for the treatment of Fragile X Syndrome.
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Inapplicable
July 01, 2024
Lead Product(s) : CTH120
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I
Sponsor : Hospital del Mar Research Institute (IMIM) | Adknoma | Ministry of Science and Innovation, Spain
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Relutrigine
Therapeutic Area : Genetic Disease
Study Phase : Phase I
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : PRAX-562 is a first selective persistent sodium current blocker. Praxis plans to initiate a Phase 2 clinical trial in the first half of 2022 to explore the potential for PRAX-562 to treat a range of rare pediatric DEEs, including SCN2A-DEE and SCN8A-DEE.
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : Inapplicable
April 30, 2021
Lead Product(s) : Relutrigine
Therapeutic Area : Genetic Disease
Highest Development Status : Phase I
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
