Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : ART4
Therapeutic Area : Genetic Disease
Study Phase : IND Enabling
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Arnatar’s ART4 Wins FDA Orphan And Rare Pediatric Disease Designations
Details : ART4 is designed to address the root cause of ALGS by upregulating endogenous JAG1 protein expression and is designed for once-monthly subcutaneous dosing.
Product Name : Undisclosed
Product Type : Oligonucleotide
Upfront Cash : Inapplicable
August 25, 2025
Lead Product(s) : ART4
Therapeutic Area : Genetic Disease
Highest Development Status : IND Enabling
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable