
01 Dec 2025
// GLOBENEWSWIRE
https://www.globenewswire.com/news-release/2025/12/01/3196939/0/en/Solid-Biosciences-Receives-FDA-Rare-Pediatric-Disease-Designation-for-SGT-212-Dual-Route-of-Administration-Gene-Therapy-for-Friedreich-s-Ataxia.html

17 Sep 2025
// PR NEWSWIRE
https://www.prnewswire.com/news-releases/skyhawk-therapeutics-announces-positive-first-interim-results-in-patients-from-its-phase-1-clinical-trial-of-sky-0515-as-a-treatment-for-huntingtons-disease-302559083.html

24 Apr 2025
// PR NEWSWIRE
https://www.prnewswire.com/news-releases/alcyone-therapeutics-announces-strategic-financing-to-advance-an-expanded-pipeline-of-pediatric-focused-precision-therapeutics-for-severe-neurological-diseases-302436946.html

24 Apr 2018
// FINANCE
https://finance.yahoo.com/news/galapagos-reports-initiation-falcon-clinical-064626530.html