Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase I/ Phase II
Sponsor : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Theranexus & BBDF Reveal Real-World Data Supporting Batten-1 for Batten
Details : Batten-1 is a novel and exclusive proprietary drug containing the active ingredient miglustat. The MOA of this substance blocks the accumulation of glycosphingolipids and neuroinflammation.
Product Name : Undisclosed
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
May 13, 2025
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase I/ Phase II
Sponsor : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : TX01
Therapeutic Area : Genetic Disease
Study Phase : Preclinical
Sponsor : Exelixis
Deal Size : Undisclosed
Deal Type : Licensing Agreement
Theranexus and Exeltis License Tx01 for Two Rare Neurological Disorders
Details : Under the licensing agreement, Exeltis will acquire exclusive rights to market and distribute Theranexus' proprietary product TX01 for treating Gaucher & Niemann-Pick Disease Type C.
Product Name : Undisclosed
Product Type : Protein
Upfront Cash : $2.1 million
December 17, 2024
Lead Product(s) : TX01
Therapeutic Area : Genetic Disease
Highest Development Status : Preclinical
Sponsor : Exelixis
Deal Size : Undisclosed
Deal Type : Licensing Agreement
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase I/ Phase II
Sponsor : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : Batten-1 is a novel and exclusive proprietary drug containing the active ingredient miglustat. The mechanism of action of this substance blocks the accumulation of glycosphingolipids and neuroinflammation. It is being investigated for CLN3 batten disease...
Product Name : Undisclosed
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
September 05, 2023
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase I/ Phase II
Sponsor : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase I/ Phase II
Recipient : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : Undisclosed
Product Name : Undisclosed
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
December 30, 2021
Lead Product(s) : Miglustat
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase I/ Phase II
Recipient : Beyond Batten Disease Foundation
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : Donepezil,Mefloquine
Therapeutic Area : Neurology
Study Phase : Phase I
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : THN201 significantly increased EEG power in the gamma band related to cognitive activity. Similar profile with respect to other pharmacological, pharmacokinetic and tolerance endpoints was observed.
Product Name : Undisclosed
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
January 15, 2020
Lead Product(s) : Donepezil,Mefloquine
Therapeutic Area : Neurology
Highest Development Status : Phase I
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : Undisclosed
Product Name : Undisclosed
Product Type : Other Small Molecule
Upfront Cash : Inapplicable
October 09, 2018
Safety and Efficacy of THN102 in Patients With Parkinson's Disease and Excessive Daytime Sleepiness
Details : Undisclosed
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Inapplicable
August 10, 2018
Impact of THN102 on Attention, Wakefulness and Cognitive Performance During Total Sleep Deprivation
Details : Undisclosed
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Inapplicable
June 09, 2017
Safety and Efficacy of THN102 on Sleepiness in Narcoleptic Patients
Details : Undisclosed
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Inapplicable
July 01, 2016