Drugs in Dev.
Rare Diseases and Disorders
Phase II
Israel 
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Lead Product(s) : MNV-201
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : MNV-201 is a Cell and Gene Therapy drug candidate, which is currently being evaluated in phase II clinical studies for the treatment of Mitochondrial Diseases.
Product Name : Undisclosed
Product Type : Cell & Gene Therapy
Upfront Cash : Inapplicable
August 30, 2023
Lead Product(s) : MNV-201
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : RZL 012
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase II
Sponsor : Fosun Pharmaceutical
Deal Size : $74.0 million
Deal Type : Licensing Agreement
Raziel Announces China Market License Agreement with Fosun Pharma for RZL 012
Details : RZL-012 is an injectable drug product indicated for aesthetic treatment of adults having moderate to significant submental fullness. Under the terms of the agreement, Raziel Therapeutics will receive potential payments between now and marketing approval ...
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : $27.0 million
September 17, 2020
Lead Product(s) : RZL 012
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase II
Sponsor : Fosun Pharmaceutical
Deal Size : $74.0 million
Deal Type : Licensing Agreement

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Lead Product(s) : RZL-012
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
RZL-012 for Dercum's Disease Lipomas
Details : RZL-012 is a Other Small Molecule drug candidate, which is currently being evaluated in phase II clinical studies for the treatment of Adiposis Dolorosa.
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : Inapplicable
January 14, 2020
Lead Product(s) : RZL-012
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Trehalose
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Treatment of Oculopharyngeal Muscular Dystrophy With Trehalose
Details : Trehalose is a Other Small Molecule drug candidate, which is currently being evaluated in phase II clinical studies for the treatment of Muscular Dystrophy, Oculopharyngeal.
Product Name : Undisclosed
Product Type : Carbohydrate
Upfront Cash : Inapplicable
January 13, 2020
Lead Product(s) : Trehalose
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable

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Lead Product(s) : Trehalose API
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : Cabaletta is a Other Small Molecule drug candidate, which is currently being evaluated in phase II clinical studies for the treatment of Muscular Dystrophy, Oculopharyngeal.
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : Inapplicable
December 19, 2013
Lead Product(s) : Trehalose API
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Phase II
Sponsor : Undisclosed
Deal Size : Inapplicable
Deal Type : Inapplicable
