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Disorders","country":"U.S.A","productType":"Vitamins\/Minerals\/Inorganic Salts","year":"2016","type":"Inapplicable","leadProduct":"Coenzyme Q10","moa":"aldosterone antagonists (spironolactone type)","graph1":"Rare Diseases and Disorders","graph2":"Phase I","graph3":"BPGbio","amount2":0,"highestDevelopmentShortName":"Ph I","therapeuticAreaShortName":"Rare Diseases","amount2New":0,"dosageForm":"Cream","sponsorNew":"BPGbio \/ Shasa Hu","highestDevelopmentStatusID":"6","companyTruncated":"BPGbio \/ Shasa Hu"},{"orgOrder":0,"company":"Takeda Pharmaceutical","sponsor":"Michael Levy","pharmaFlowCategory":"DU","therapeuticArea":"Rare Diseases and Disorders","country":"JAPAN","productType":"Undisclosed","year":"2013","type":"Inapplicable","leadProduct":"C1 Esterase Inhibitor, Human","moa":"C1 esterase","graph1":"Rare Diseases and Disorders","graph2":"Phase I","graph3":"Takeda Pharmaceutical","amount2":0,"highestDevelopmentShortName":"Ph I","therapeuticAreaShortName":"Rare Diseases","amount2New":0,"dosageForm":"Undisclosed","sponsorNew":"Takeda Pharmaceutical \/ Michael Levy","highestDevelopmentStatusID":"6","companyTruncated":"Takeda Pharmaceutical \/ Michael Levy"},{"orgOrder":0,"company":"Ultragenyx Pharmaceutical","sponsor":"Jirair Krikor Bedoyan","pharmaFlowCategory":"DU","therapeuticArea":"Rare Diseases and Disorders","country":"U.S.A","productType":"Miscellaneous","year":"2024","type":"Inapplicable","leadProduct":"Triheptanoin","moa":"Triglyceride","graph1":"Rare Diseases and Disorders","graph2":"Phase I","graph3":"Ultragenyx Pharmaceutical","amount2":0,"highestDevelopmentShortName":"Ph I","therapeuticAreaShortName":"Rare Diseases","amount2New":0,"dosageForm":"Undisclosed","sponsorNew":"Ultragenyx Pharmaceutical \/ Jirair Krikor Bedoyan","highestDevelopmentStatusID":"6","companyTruncated":"Ultragenyx Pharmaceutical \/ Jirair Krikor Bedoyan"}]
Find Drugs for Rare Diseases and Disorders in Phase I Clinical Development in UNITED STATES
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