Drugs in Dev.
Rare Diseases and Disorders
Discovery
Japan 
Boost your online visibility by uploading your products, APIs, FDFs, intermediates, excipients, and services for free on PharmaCompass.
Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Sponsor : AMED
Deal Size : $0.3 million
Deal Type : Funding
RevolKa Joins R&D Program for Innovative Biologics Funded by the Japanese AMED
Details : RevolKa’s platform, ai Protein, uses AI-driven, directed evolution techniques to engineer novel proteins with therapeutic potential for rare diseases.
Product Name : Undisclosed
Product Type : Protein
Upfront Cash : Undisclosed
June 30, 2025
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Sponsor : AMED
Deal Size : $0.3 million
Deal Type : Funding

Boost your online visibility by uploading your products, APIs, FDFs, intermediates, excipients, and services for free on PharmaCompass.
Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : RKD001
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Sponsor : DEEPCORE
Deal Size : $1.7 million
Deal Type : Series A Financing
RevolKa Closes $1.7M Series A Extension To Advance Drug Discovery
Details : The proceeds will accelerate RevolKa’s drug discovery and development activities, including RKD001, a protein in discovery for rare diseases.
Product Name : Undisclosed
Product Type : Miscellaneous
Upfront Cash : Undisclosed
August 29, 2024
Lead Product(s) : RKD001
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Sponsor : DEEPCORE
Deal Size : $1.7 million
Deal Type : Series A Financing

Boost your online visibility by uploading your products, APIs, FDFs, intermediates, excipients, and services for free on PharmaCompass.
Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Sponsor : Kyowa Kirin
Deal Size : Undisclosed
Deal Type : Collaboration
Details : LUCA Science will use its proprietary platform technology to manufacture, store and deliver innovative mitochondrial drugs to research and development of therapeutics for unmet medical needs in a wide range of diseases for which there have been no effect...
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Undisclosed
May 18, 2022
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Sponsor : Kyowa Kirin
Deal Size : Undisclosed
Deal Type : Collaboration

Boost your online visibility by uploading your products, APIs, FDFs, intermediates, excipients, and services for free on PharmaCompass.
Rank higher among suppliers and expand your reach across the internet efficiently and cost-effectively.
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Sponsor : Carmine Therapeutics
Deal Size : $900.0 million
Deal Type : Collaboration
Takeda Partners up with Carmine Therapeutics to Develop and Market Rare Disease Candidates
Details : The collaboration will leverage Carmine’s REGENT technology, which is based on red blood cell extracellular vesicles, allowing for repeat dosing, enhanced bio-distribution and larger transgene payload capacity compared to adeno-associated virus-based g...
Product Name : Undisclosed
Product Type : Undisclosed
Upfront Cash : Undisclosed
June 30, 2020
Lead Product(s) : Undisclosed
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Sponsor : Carmine Therapeutics
Deal Size : $900.0 million
Deal Type : Collaboration
