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            Lead Product(s): LentiGlobin Gene Therapy

            Therapeutic Area: Genetic Disease Product Name: Bb1111

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable December 07, 2020

            Details:

            Positive patient-reported quality of life outcomes assessed with validated PROMIS-57 demonstrate clinically meaningful reductions in pain intensity at Month 12 post-LentiGlobin for SCD treatment.

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            Lead Product(s): OTL-200

            Therapeutic Area: Genetic Disease Product Name: OTL-200

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable November 19, 2020

            Details:

            FDA has cleared the company’s Investigational New Drug application for OTL-200, an autologous, hematopoietic stem cell, lentiviral vector-based gene therapy in development for the treatment of metachromatic leukodystrophy.

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            Lead Product(s): LentiGlobin,Plerixafor

            Therapeutic Area: Genetic Disease Product Name: BB305

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable November 04, 2020

            Details:

            bluebird bio announces confirmation of its general agreement with the U.S.FDA that the clinical data package required to support a BLA submission for LentiGlobin™ for sickle cell disease will be based on data from a portion of patients in the HGB-206 study Group C.

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            Lead Product(s): Libmeldy

            Therapeutic Area: Genetic Disease Product Name: OTL-200

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable November 03, 2020

            Details:

            Libmeldy TM receives positive CHMP opinion for the treatment of Early-onset metachromatic leukodystrophy (MLD); U.S. IND application on Track for Year End 2020.

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            Lead Product(s): Libmeldy

            Therapeutic Area: Genetic Disease Product Name: OTL-200

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable October 16, 2020

            Details:

            The CHMP’s positive opinion will now be reviewed by the European Commission (EC), which has the authority to grant marketing authorization for Libmeldy in the European Union (EU).

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            Lead Product(s): Elivaldogene autotemcel

            Therapeutic Area: Genetic Disease Product Name: Lenti-D

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable October 02, 2020

            Details:

            Data from the Phase 2/3 Starbeam study (ALD-102) formed the basis of the MAA, which is also supported with data from the ongoing Phase 3 ALD-104 study and the long-term follow-up study (LTF-304).

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            Lead Product(s): LentiGlobin

            Therapeutic Area: Genetic Disease Product Name: BB305

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable September 23, 2020

            Details:

            Clinical data from the completed Phase 1/2 HGB-205 study, the ongoing Phase 1/2 HGB-206 study and ongoing long-term safety and efficacy follow-up study LTF-303 supported the PRIME application for LentiGlobin for SCD.

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            Lead Product(s): Elivaldogene autotemcel

            Therapeutic Area: Genetic Disease Product Name: Lenti-D

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable August 29, 2020

            Details:

            Bluebird bio is currently enrolling patients for ALD-104, a Phase 3 study designed to assess the efficacy and safety of eli-cel in patients with CALD after myeloablative conditioning using busulfan and fludarabine.

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            Lead Product(s): Elivaldogene autotemcel

            Therapeutic Area: Genetic Disease Product Name: Lenti-D

            Highest Development Status: Phase III Product Type: Cell and Gene therapy

            Partner/Sponsor/Collaborator: Not Applicable

            Deal Size: Not Applicable Upfront Cash: Not Applicable

            Deal Type: Not Applicable August 17, 2020

            Details:

            Data from the clinical development program for its investigational elivaldogene autotemcel gene therapy in patients with cerebral adrenoleukodystroph, including data from the Phase 2/3 Starbeam study and Phase 3 ALD-104 study, will be presented at the 46th Annual EBMT 2020.