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    [{"orgOrder":0,"company":"Enzyvant","sponsor":"Aceragen","pharmaFlowCategory":"D","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Enzyme","year":"2021","type":"Acquisition","leadProduct":"Recombinant Human Acid Ceramidase","moa":"Acid ceramidase","graph1":"Genetic Disease","graph2":"IND Enabling","graph3":"Enzyvant","amount2":0,"highestDevelopmentShortName":"IND","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Undisclosed","sponsorNew":"Enzyvant \/ Aceragen","highestDevelopmentStatusID":"5","companyTruncated":"Enzyvant \/ Aceragen"}]

    Find Genetic Disease Clinical Drug Pipeline Developments & Deals by Enzyvant

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                            Lead Product(s) : Recombinant Human Acid Ceramidase

                            Therapeutic Area : Genetic Disease

                            Study Phase : IND Enabling

                            Sponsor : Aceragen

                            Deal Size : $226.0 million

                            Deal Type : Acquisition

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                            Aceragen Launches with Acquisition of Enzyvant‘s Investigational Therapy for Farber Disease

                            Details : ACG-801 is an investigational form of recombinant human acid ceramidase (rhAC) designed to address the genetic deficiency of the naturally occurring enzyme which is the cause of Farber disease and Spinal Muscular Atrophy with Progressive Myoclonic Epilep...

                            Product Name : ACG-801

                            Product Type : Enzyme

                            Upfront Cash : Undisclosed

                            March 05, 2021

                            Lead Product(s) : Recombinant Human Acid Ceramidase

                            Therapeutic Area : Genetic Disease

                            Highest Development Status : IND Enabling

                            Sponsor : Aceragen

                            Deal Size : $226.0 million

                            Deal Type : Acquisition

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