Lead Product(s) : ARO-DM1
Therapeutic Area : Neurology
Study Phase : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Arrowhead Pharmaceuticals Starts Phase 1/2a Study of ARO-DM1 for Type 1 Myotonic Dystrophy
Details : ARO-DM1 is designed to reduce expression of the dystrophia myotonica protein kinase (DMPK) gene in the muscle. It is being evaluated for the treatment of type 1 myotonic dystrophy.
Product Name : ARO-DM1
Product Type : Oligonucleotide
Upfront Cash : Inapplicable
August 03, 2024
Lead Product(s) : ARO-DM1
Therapeutic Area : Neurology
Highest Development Status : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : ARO-DM1
Therapeutic Area : Neurology
Study Phase : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : ARO-DM1 is designed to reduce expression of the dystrophia myotonica protein kinase (DMPK) gene in the muscle. It is being evaluated for the treatment of type 1 myotonic dystrophy.
Product Name : ARO-DM1
Product Type : Oligonucleotide
Upfront Cash : Inapplicable
November 28, 2023
Lead Product(s) : ARO-DM1
Therapeutic Area : Neurology
Highest Development Status : Phase I/ Phase II
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : ARO-SOD1
Therapeutic Area : Neurology
Study Phase : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Arrowhead Pharmaceuticals Files for Regulatory Clearance to Initiate a Phase 1 Study of ARO-SOD1
Details : ARO-SOD1, an RNAi-based investigational medicine designed to reduce expression of superoxide dismutase 1 (SOD1) in the central nervous system (CNS) as a potential treatment for patients with amyotrophic lateral sclerosis (ALS) caused by SOD1 mutations.
Product Name : ARO-SOD1
Product Type : Other Large Molecule
Upfront Cash : Inapplicable
June 27, 2023
Lead Product(s) : ARO-SOD1
Therapeutic Area : Neurology
Highest Development Status : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable